TY  - JOUR
AU  - Marcos Ramiro, Beatriz
AU  - Gil Ordóñez, Ana
AU  - Marín Ramos, Nagore I.
AU  - Ortega Nogales, Francisco J.
AU  - Balabasquer, Moisés
AU  - Gonzalo, Pilar
AU  - Ortega Gutiérrez, Silvia
AU  - Khiar Fernández, Nora
AU  - Rolas, Loic
AU  - Barkaway, Anna
AU  - Nourshargh, Sussan
AU  - Andrés, Vicente
AU  - Martín-Fontecha Corrales, María Del Mar
AU  - López Rodríguez, María Luz
PY  - 2021
DO  - 10.1021/acscentsci.0c01698
SN  - 2374-7943
UR  - https://hdl.handle.net/20.500.14352/102561
T2  - ACS Central Science
AB  - Hutchinson–Gilford progeria syndrome (HGPS, progeria) is a rare genetic disease characterized by premature aging and death in childhood for which there were no approved drugs for its treatment until last November, when lonafarnib obtained long-sought...
LA  - eng
M2  - 1300
PB  - ACS Publications
KW  - Assays
KW  - Genetics
KW  - Inhibitors
KW  - Peptides and proteins
KW  - Rodent models
TI  - Isoprenylcysteine Carboxylmethyltransferase-Based Therapy for Hutchinson−Gilford Progeria Syndrome
TY  - journal article
VL  - 7
ER  -