TY  - JOUR
AU  - Serrano Ramos, Luis Javier
AU  - García Arranz, Mariano
AU  - De Pablo Moreno, Juan Andrés
AU  - Segovia, José Carlos
AU  - Olivera Salazar, Rocío
AU  - García Olmo, Damián
AU  - Liras Martín, Antonio
PY  - 2022
DO  - 10.3390/ijms23105802
SN  - 1661-6596
UR  - https://hdl.handle.net/20.500.14352/110863
T2  - International Journal of Molecular Sciences
AB  - Factor V deficiency, an ultra-rare congenital coagulopathy, is characterized by bleeding episodes that may be more or less intense as a function of the levels of coagulation factor activity present in plasma. Fresh-frozen plasma, often used to treat...
LA  - eng
M2  - 1
PB  - MDPI
KW  - Gene therapy
KW  - Gene editing
KW  - CRISPR
KW  - Factor V deficiency
KW  - Coagulopathies
KW  - Rare diseases
TI  - Development and characterization of a factor V‐deficient CRISPR cell model for the correction of mutations
TY  - journal article
VL  - 23
ER  -