TY - JOUR AU - Ortega Gutiérrez, Silvia PY - 2023 DO - 10.3390/ijms24087275 SN - 1422-0067 UR - https://hdl.handle.net/20.500.14352/109794 T2 - Internationl Journal of Molecular Sciences AB - The expression “rare disease” describes a group of diseases whose individual prevalence is low (between 3.9 and 6.6 in 10,000 subjects depending on the country) but which in total affect up to the 3–6% of the worldwide population. LA - eng M2 - 7275 PB - MDPI TI - New pharmacological approaches for rare diseases TY - journal article VL - 24 ER -