TY  - JOUR
AU  - Liras, Antonio
AU  - Segovia, Cristina
AU  - Gaban, Aline S.
PY  - 2012
DO  - 10.1186/1750-1172-7-97
SN  - 1750-1172, 1750-1172(ESSN)
UR  - https://hdl.handle.net/20.500.14352/44628
T2  - Orphanet journal of rare diseases
AB  - Monogenic diseases are ideal candidates for treatment by the emerging advanced therapies, which are capable of correcting alterations in protein expression that result from genetic mutation. In hemophilia A and B such alterations affect the activity...
LA  - eng
M2  - 1
PB  - BioMed Central
KW  - Advanced therapies
KW  - Gene therapy
KW  - Cell therapy
KW  - Hemophilia A
KW  - Hemophilia B
TI  - Advanced therapies for the treatment ofhemophilia: future perspectives
TY  - journal article
VL  - 7
ER  -