Ortega Gutiérrez, Silvia2024-10-302024-10-302023Int. J. Mol. Sci. 2023, 24(8), 7275; https://doi.org/10.3390/ijms240872751422-006710.3390/ijms24087275https://hdl.handle.net/20.500.14352/109794The expression “rare disease” describes a group of diseases whose individual prevalence is low (between 3.9 and 6.6 in 10,000 subjects depending on the country) but which in total affect up to the 3–6% of the worldwide population.engAttribution-NonCommercial-NoDerivatives 4.0 Internationalhttp://creativecommons.org/licenses/by-nc-nd/4.0/New pharmacological approaches for rare diseasesjournal articlehttps://doi.org/10.3390/ijms24087275open access547Química orgánica (Química)2306 Química Orgánica